Polish diagnostician Dr. Jaroslaw Wilczynski says to look beyond symptoms, analyze the data and admit where things go wrong ...

The FDA will submit a boxed warning and other labeling limits for Elevidys, an adeno-associated virus and vector-based gene ...

As most sources of drinking water contain markers of certain heavy metals and pollutants that settle on the surface due to ...

I’ve been reflecting on the disappointing outcomes and the reaction to Sarepta Therapeutics’ recently announced clinical ...

SMA expert Brian Lin, PhD, shares his thoughts on aging with SMA, treatment, advocacy, and supporting patients across their ...

SMA expert Brian Lin, PhD, shares his thoughts on aging with SMA, treatment, advocacy, and supporting patients across their ...

They face a difficult choice, since the treatment may benefit their children but comes with serious risks and unknowns, particularly following reports of patient deaths.

Elevidys now carries a black box warning for acute liver injury and failure, limiting its use to ambulatory patients aged four and older. The FDA's actions follow fatal liver failure reports in ...

The recommendation is based on the Phase II/III DEVOTE study testing the higher dose in treatment-naïve patients and those already on the low dose.

Sarepta must also run a post-marketing study for Elevidys to better assess the risk of serious liver injury in patients dosed ...

MONDAY, Nov. 17, 2025 (HealthDay News) — The U.S. Food and Drug Administration (FDA) is tightening restrictions on a gene ...

Here are the three best exercises for building muscle, according to research (and experts): Squats “mimic many of our ...